Latest news stories about centronuclear and myotubular myopathy can be found on this page. To see news stories from previous years please see the News archive pages.
- Audentes Therapeutics Reports Third Death In A Clinical Trial
Technologytimes.pk, 22 August 2020 - Audentes Therapeutics Provides Update on the ASPIRO Clinical Trial Evaluating AT132 in Patients with X-linked Myotubular Myopathy
Pipelinereview.com, 21 August 2020 - Astellas’ Audentes reports 3rd death in gene therapy trial
Fiercebiotech.com, 21 August 2020 - Audentes Therapeutics provides update on the ASPIRO clinical trial evaluating AT132 in patients with X-linked myotubular myopathy
Business Wire, 21 August 2020 - Audentes Therapeutics Provides Update on the ASPIRO Clinical Trial Evaluating AT132 in Patients with X-linked Myotubular Myopathy
Audentes, 20 August 2020 - Dynacure receives rare pediatric disease designation from U.S. Food and Drug Administration for DYN101 for myotubular and centronuclear myopathies (CNM)
prnewswire.com, 30 July 2020 - Dynacure receives rare pediatric disease designation from U.S. Food and Drug Administration for DYN101 for myotubular and centronuclear myopathies
Dynacure, 30 July 2020 - Guard of honour and police motorbike escort for four year old boy after 14 months in hospital
ITV News, 24 July 2020 - Liverpool guard of honour after Hari’s long hospital stay
BBC News, 24 July 2020 - Caernarfon boy with myotubular myopathy leaves hospital
BBC News, 24 July 2020 - Hari Jones, who suffers from a rare muscular condition, returned home to Caernarfon from Alder Hey Children’s Hospital and was met with a police escort
North Wales Chronicle, 22 July 2020 - Tears outside hospital as little boy finally leaves after 14 months
Liverpool Echo, 22 July 2020 - On Being BOLD
LinkedIn, 10 July 2020 - Gene Therapy: It’s Time to Talk about High-Dose AAV
Genetic Engineering and Biotechnology News, 7 July 2020 - Concern following gene therapy adverse events
Medical Xpress, 2 July 2020 - Moving Forward after Two Deaths in a Gene Therapy Trial of Myotubular Myopathy
Genetic Engineering and Biotechnology News, 2 July 2020 - Audentes halts gene therapy trial after second patient death
The Pharma Letter, 30 June 2020 - Two boys’ deaths halt S.F. company’s rare disease gene therapy trial
Biz Journals, 29 June 2020 - Two patients die in Audentes gene therapy study, heightening concerns over high-dose treatments
Stat News, 28 June 2020 - Two patients die in Audentes gene therapy study, heightening concerns over high-dose treatments
Bio Pharma Dive, 26 June 2020 - Amid a Pandemic, Photographers Help Grieving Parents Find Hope Through Suffering
The Federalist, 6 April 2020 - Dynacure Adds $55M As RNA-Targeted Muscle Disorder Drug Enters Clinic
Xconomy, 3 April 2020 - Dynacure Announces €50M ($55M) Series C Financing
Biospace, 2 April 2020 - Dynacure Announces €50M ($55M) Series C Financing
Dynacure, 2 April 2020 - Dynacure Announces EUR50M ($55M) Series C Financing
P and T Community, 2 April 2020 - Funding supports ongoing Phase 1 / 2 ‘Unite-CNM’ study of DYN101 in Patients with Myotubular and Centronuclear Myopathies
Yahoo Finance, 2 April 2020 - An ’emergency’ birthday party for ten year old Cork boy
RTE News, 1 April 2020 - Dynacure Announces First Patient Dosed in Phase 1 / 2 ‘UNITE-CNM’ Study of DYN101 for the Treatment of Myotubular and Centronuclear Myopathies (CNM)
P and T Community, 5 March 2020 - Dynacure Announces First Patient Dosed in Phase 1 / 2 ‘UNITE-CNM’ Study of DYN101 for the Treatment of Myotubular and Centronuclear Myopathies (CNM)
BioSpace, 5 March 2020 - Dynacure Announces First Patient Dosed in Phase 1 / 2 ‘UNITE-CNM’ Study of DYN101 for the Treatment of Myotubular and Centronuclear Myopathies (CNM)
Dynacure, 5 March 2020 - Here’s how you can get involved in The Big Sunflower Project
Liverpool Echo, 4 March 2020 - Two Aurora Health Children’s patients head to meet the Brewers at Spring Training
TMJ4.com, 21 February 2020 - Family of twins call for change to DLA Motability scheme
Leigh Journal, 13 February 2020 - New insights from Mack Lab on mechanisms of gene therapy for x-linked myotubular myopathy
Institute for Stem Cell and Regenerative Medicine, 5 February 2020 - Chester-based Big Sunflower Project continues to grow in its 10th year
Chester Standard, 21 January 2020 - Astellas completes acquisition of Audentes Therapeutics
Audentes, 15 January 2020 - Astellas, Audentes merger may lead to new exon-skipping treatments for MD
Muscular Dystrophy News Today, 6 January 2020
